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ANCA-associated vasculitis

ANCA-associated vasculitis is a rare inflammatory disease of the blood vessels that can compromise tissue perfusion and damage multiple organs

Prevalence

~40–50 / 100,000

US Estimated

~10–30 / 100,000

Europe Estimated

Age of Onset

Adults

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ICD-10

I77.82

Inheritance Pattern

Autosomal dominant

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Autosomal recessive

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Mitochondrial/Multigenic

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X-linked dominant

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X-linked recessive

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5 Facts you should know

FACT

1

ANCA-Associated Vasculitis (AAV) comprises a group of autoimmune diseases affecting small blood vessels, including granulomatosis with polyangiitis (GPA), microscopic polyangiitis (MPA), and eosinophilic granulomatosis with polyangiitis (EGPA)

FACT

2

Onset typically occurs in middle age, with a peak incidence between 50 to 70 years old

FACT

3

Symptoms may include constitutional symptoms like fatigue, fever, weight loss, and general malaise

FACT

4

Common clinical manifestations involve the respiratory tract (sinusitis, pulmonary infiltrates), kidneys (hematuria, proteinuria), and systemic involvement (nerve damage, skin lesions)

FACT

5

Diagnosis involves clinical evaluation, serological testing for ANCA antibodies, imaging studies, and biopsy to confirm vasculitis

ANCA-associated vasculitis is also known as...

ANCA-associated vasculitis is also known as:

  • AAV

  • Anti-neutrophil cytoplasmic antibody-associated vasculitis

  • Antineutrophil cytoplasmic antibody-associated vasculitis

What’s your Rare IQ?

Which antibodies are predominantly associated with ANCA-Associated Vasculitis?

 

Common signs & symptoms

Constitutional

  • Fever, weight loss, fatigue

ENT involvement

  • Chronic sinusitis, otitis media, nasal crusting or epistaxis

Pulmonary manifestations

  • Cough, dyspnea, pulmonary infiltrates, alveolar hemorrhage (subtype-dependent)

Renal involvement

  • Hematuria, proteinuria, rapidly progressive glomerulonephritis

Skin findings

  • Palpable purpura, livedo, ulcers

Neurologic involvement

  • Mononeuritis multiplex or peripheral neuropathy

Clinical presentation varies across GPA, MPA, and EGPA

Current treatments

Induction therapy

Systemic glucocorticoids combined with rituximab or cyclophosphamide, depending on disease severity and organ involvement

Steroid-sparing therapy

Avacopan (C5a receptor inhibitor) in selected patients, with guideline-recommended limited duration

Maintenance therapy

Rituximab or conventional immunosuppressive agents to reduce relapse risk

Treatment strategy is guided by disease subtype, severity, and organ involvement